Expanded Access Protocol to Provide Patisiran to Patients

Recruiting

99 years or below

All

1 Location

Brief description of study

This patisiran expanded access protocol (EAP) is an open-label, multicenter, single-arm study designed to provide pre-approval access to investigational patisiran for patients with ATTR amyloidosis with cardiomyopathy who, at baseline, have an inadequate response to or cannot tolerate standard of care. An intravenous infusion of study drug (patisiran 0.3 mg/kg) will be administered once every 3 weeks until the drug is commercially available or until the Sponsor terminates the study.

Eligibility of study

You may be eligible for this study if you meet the following criteria:

Conditions: Medical Research
Age: 99 years or below
Gender: All

Updated on 08 Mar 2023. Study ID: 851365

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Expanded Access Protocol to Provide Patisiran to Patients with Transthyretin-mediated Amyloidosis (ATTR Amyloidosis) with Cardiomyopathy

Brief description of study

Eligibility of study

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