A Randomized Study to Evaluate the Efficacy and Safety of ION-682884 in Patients with Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
Recruiting
18 years - 82 years
All
Phase
3
140 participants needed
1 Location
Brief description of study
A Phase 3 Global, Open-Label, Randomized Study to Evaluate the Efficacy and Safety of ION-682884 in Patients with Hereditary Transthyretin-Mediated Amyloid Polyneuropathy. For those with :
a. Stage 1 or Stage 2 according to the Familial Amyloid Polyneuropathy (FAP) or Coutinho Stage
b. Documented genetic mutation in the TTR gene
c. Symptoms and signs consistent with neuropathy associated with
transthyretin amyloidosis
Eligibility of study
You may be eligible for this study if you meet the following criteria:
- Conditions: Transthyretin-Mediated Amyloid Polyneuropathy,neuropathy,
-
Age: 18 years - 82 years
-
Gender: All
Male or Female Age 18-82 a. Stage 1 or Stage 2 according to the Familial Amyloid Polyneuropathy (FAP) or Coutinho Stage b. Documented genetic mutation in the TTR gene c. Symptoms and signs consistent with neuropathy associated with, transthyretin.
Updated on
04 Aug 2024.
Study ID: 834496