Found 107 Muscular Dystrophy trials
A listing of Muscular Dystrophy medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.
A Study to Assess the Safety and Efficacy of a Subcutaneous Formulation of Efgartigimod in Adults With Chronic Inflammatory Demyelinating Polyneuropathy ( (ADHERE)
Study to evaluate the safety and efficacy of the subcutaneous formulation of efgartigimod in adults with CIDP.
Safety and Efficacy Study of Ravulizumab in Adults With Generalized Myasthenia Gravis
The primary purpose of this study is to evaluate the safety and efficacy of ravulizumab for the treatment of participants with generalized myasthenia gravis (gMG).
Effect of Dapagliflozin on Submaximal Exercise Tolerance in Heart Failure
The primary purpose of this study is to test whether the dapagliflozin (Dapa) will improve exercise duration in people with Heart Failure (HF). In HF, patients are limited in their ability to do all the things they want to do, and exercise as much as they would like, due to …
Human Heart Tissue Protocol
The broad objective of this proposed research protocol is to have heart tissue specimens available to use for studies designed to help us better understand the causes and manifestations of human heart failure. The broad objective of this proposed research protocol is to have heart tissue specimens available to use …
Efficacy and Safety of M281 in Adults with Warm Autoimmune Hemolytic Anemia: A Multicenter Randomized Double blind Placebo controlled Study with a Long-term Open-label Extension
Efficacy of nipocalimab in patients with warm autoimmune hemolytic anemia (wAIHA) Durable response in improvement in hemoglobin (Hgb), defined as attainment of the following at 3 consecutive visits, where at least the first is at or before Week 16, without the need of rescue therapy: 1- Hgb concentration greater than …
A Phase 2a Randomized Placebo-Controlled Clinical Study to Evaluate the Efficacy and Safety of MK-5475 in Adults With Pulmonary Hypertension Associated With Chronic Obstructive Pulmonary Disease
This study will assess MK5475 in patients with PH related to COPD. Patients will undergo the following procedures: medical history, lab testing, lung function testing, a CT, EKGs, an echocardiogram, heart catheterization, and 6MWTs.
Detection and Characterization of Subclinical Atherosclerotic Plaques in High-Risk Populations of Lupus Erythematosus and Dermatomyositis Patients: A Prospective Single-Center Cohort Study
To determine the burden of subclinical coronary and iliofemoral arterial plaque in 30- to 50-year-old patients with lupus erythematosus (LE) or dermatomyositis (DM) but no clinically evident atherosclerotic cardiovascular disease (ASCVD); and to determine the nature, location, and characteristics of subclinical plaques in these patients. To detect the extent and …
Retrospective and Prospective Evaluation of Hip Short Stem Performed by Anterior Approach (AMISP)
This study aims to evaluate the clinical, radiographic, and perioperative outcomes of short femoral stems implanted during primary total hip arthroplasty performed through a minimally invasive direct anterior approach (DAA). Short femoral stems have been developed to preserve proximal femoral bone stock, potentially provide a more physiological load transfer, and …
A Pilot Study of Diffusion Weighted MRI to Assess Esophageal Tumor Response to Neoadjuvant Chemoradiation
The purpose of this study is to determine if a particular Magnetic Resonance Imaging (MRI) called Diffusion Weighted (dwMRI)) will detect changes in your tumor before and during treatment with chemotherapy and radiation for esophageal cancer. We used the dwMRI because it has been used in other types of cancers …
A Phase 3 Double-Blind Randomized Placebo-Controlled Multicenter Study to Evaluate the Efficacy and Safety of Obeticholic Acid in Subjects with Compensated Cirrhosis due to Nonalcoholic Steatohepatitis
A Phase 3, Double-Blind, Randomized, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of Obeticholic Acid in Subjects with Compensated Cirrhosis due to Nonalcoholic Steatohepatitis
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